Search results for #RareDiseases
EATRIS is excited to be an Associate Partner of #ECRD2024 - the European Conference for #RareDiseases & Orphan Products taking place in Brussels on 15-16 May 2024 & online. Hosted by the patient-driven rare disease alliance @eurordis. 👉 More here: eatris.eu/events/12th-eu…
Contestant makes history as first Miss Delaware Teen USA with Down syndrome #RareDiseases #DownSyndromeAwareness #DownSyndromeCommunity [Video] History was made in Delaware Sunday night, as 17-year-old Kayla Kosmalski became the first contestant with… dlvr.it/T6F0S1
Join us for this @ASGCTherapy Core Curriculum Series & earn free #CME credit! Hear from field experts on how cell & gene based therapies can change the disease course of genetic conditions/cancers ➡️ bit.ly/3QpgHVG @RareDiseases #GeneTherapy #CellTherapy #RareDiseases
Huge thanks & admiration for @mattgoss who so kindly shared a message of hope & courage to those living with Poland Syndrome … breaking down the stigma & lack of understanding so brilliantly - thx @OK_Magazine ⭐️ #polandSyndrome #showbiz #celebrity #rarediseases #health…
Hemophilia a condition which causes excessive blood lose in women after birth #RareDiseases #FragileXSyndromeCommunity #FragileXSyndromeEducation #FragileXSyndromeInclusion [Video] Hemophilia a condition which causes excessive blood lose in women after ... dlvr.it/T6Dl4G
BEC and @AgiosPharma are #partnering to expand their sales organization, introducing life-changing therapies to make a difference the lives of individuals with #RareDiseases. #Pharmaceutical #Recruiting
Alterity Therapeutics Presents New Data Demonstrating Potential of ATH434 to Treat Rare Neurodegenerative Disease Friedreich’s Ataxia - please check the link for more details ow.ly/V0cX50RsB5L @AlterityT #FriedreichsAtaxia #Neurology #RareDiseases #FDA
#SynBioBeta2024 is one week away! Putting together your itinerary? Don’t miss our panel on May 7th at 1:45pm PT about the next frontiers in protein & nucleic acid medicines. See the full agenda @SynBioBeta: web.cvent.com/event/7ff628c3… #tRNA #RNA #rarediseases #geneticmedicines
#SynBioBeta2024 is one week away! Putting together your itinerary? Don’t miss our panel on May 7th at 1:45pm PT about the next frontiers in protein & nucleic acid medicines. See the full agenda @SynBioBeta: web.cvent.com/event/7ff628c3… #tRNA #RNA #rarediseases #geneticmedicines
Ultragenyx Announces Completion of Enrollment in Phase 3 Orbit and Cosmic Studies Evaluating Setrusumab (UX143) in the Treatment of Osteogenesis Imperfecta - check the link for more info ow.ly/SaOW50RsqVk @ultragenyx #OsteogenesisImperfecta #RareDiseases
✈️ Heading to #ASGCT24 next month? Ask us how we can support your upcoming research endeavors and explore our wide range of capabilities and services at booth 2172! noblelifesci.com/asgct-27th-ann… #ASGCT #celltherapy #cellandgene #rarediseases #genetherapy #toxicology
A glimpse into the pipeline for new therapies is always a highlight of our orphan drug report. For a quick read of the key takeaways, the team at Fierce Pharma has written this handy article. ow.ly/8rmG50RsAi1 #Pharma #RareDiseases
This PR urges US-India collaboration to advance #newbornscreening for #rarediseases. Dr. @Harsharajasimha, Ph.D., talks on broader screening, innovative tech, & removing barriers. Read this @prweb article: buff.ly/3UEKYSZ Contact Us: buff.ly/3PZaxeM #indousrare